ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
ASPsiRNA ID | Mutant allele/ASP-siRNA | Efficacy for mutant(%) |
Efficacy for wild (%) |
Relative Difference (%) | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
aspsirna3435 | GGGACAGUAAUUCAACGCUU CCCUGUCAUUAAGUUGCGAA |
85 | 10 | 75 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3436 | GUAAUUCAACGCUAGAA CAUUAAGUUGCGAUCUU |
90 | 10 | 80 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3437 | GUACUUCAACGCUAGAAGAU CAUGAAGUUGCGAUCUUCUA |
88 | 15 | 73 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3438 | GGGACAGUACUUCAACGCUU CCCUGUCAUGAAGUUGCGAA |
80 | 5 | 75 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3445 | GGGACAGUAAUUCAACGCUU CCCUGUCAUUAAGUUGCGAA |
80 | 20 | 60 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3446 | GUAAUUCAACGCUAGAA CAUUAAGUUGCGAUCUU |
100 | 40 | 60 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3447 | GUACUUCAACGCUAGAAGAU CAUGAAGUUGCGAUCUUCUA |
78 | 20 | 58 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3448 | GGGACAGUACUUCAACGCUU CCCUGUCAUGAAGUUGCGAA |
80 | 5 | 75 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3455 | GGGACAGUAAUUCAACGCUU CCCUGUCAUUAAGUUGCGAA |
98 | 60 | 38 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3456 | GUAAUUCAACGCUAGAA CAUUAAGUUGCGAUCUU |
100 | 40 | 60 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3457 | GUACUUCAACGCUAGAAGAU CAUGAAGUUGCGAUCUUCUA |
78 | 20 | 58 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3458 | GGGACAGUACUUCAACGCUU CCCUGUCAUGAAGUUGCGAA |
97 | 67 | 30 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3465 | GGGACAGUAAUUCAACGCUU CCCUGUCAUUAAGUUGCGAA |
98 | 60 | 38 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3466 | GUAAUUCAACGCUAGAA CAUUAAGUUGCGAUCUU |
100 | 40 | 60 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3467 | GUACUUCAACGCUAGAAGAU CAUGAAGUUGCGAUCUUCUA |
78 | 20 | 58 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3468 | GGGACAGUACUUCAACGCUU CCCUGUCAUGAAGUUGCGAA |
97 | 67 | 30 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3475 | GGGACAGUAAUUCAACGCUU CCCUGUCAUUAAGUUGCGAA |
98 | 28 | 70 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3476 | GUAAUUCAACGCUAGAA CAUUAAGUUGCGAUCUU |
100 | 40 | 60 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3477 | GUACUUCAACGCUAGAAGAU CAUGAAGUUGCGAUCUUCUA |
78 | 20 | 58 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3478 | GGGACAGUACUUCAACGCUU CCCUGUCAUGAAGUUGCGAA |
97 | 30 | 67 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3485 | GGGACAGUAAUUCAACGCUU CCCUGUCAUUAAGUUGCGAA |
70 | 30 | 40 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3486 | GUAAUUCAACGCUAGAA CAUUAAGUUGCGAUCUU |
98 | 40 | 58 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3487 | GUACUUCAACGCUAGAAGAU CAUGAAGUUGCGAUCUUCUA |
88 | 20 | 68 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 | ||
aspsirna3488 | GGGACAGUACUUCAACGCUU CCCUGUCAUGAAGUUGCGAA |
97 | 67 | 30 | HTT | Huntington disease (HD) | NM_002111.7:c.5165C>A | rs363125 |